New gene therapy fetches $1.8m for one shot, among costly 'miracle cures'

Scientists have been making major breakthroughs in the treatment of genetic disorders.

Gene therapy is an experimental technique that uses genes to treat or prevent genetic disease.

This medical advancement will soon allow doctors to treat a disorder by inserting a gene into a patient's cells instead of using drugs or surgery.

Pharmaceutical companies worldwide are racing to be at the forefront of gene therapy with single-dose treatments.

But potential genetic cures don't come cheap, with some costing as much as $1,8 million (R26,84 million) per person for a single treatment.

Bloomberg healthcare journalist James Paton conducted an investigative report into the high cost of a one-shot therapy used to treat a condition called beta thalassemia.

Beta thalassemia is a genetic disorder that hampers red blood cells’ ability to carry oxygen through the body.

Many patients with condition need regular blood transfusions to survive.

Paton says the $1,8 million price tag presents a serious challenge to the hope given by these genetic treatments.

He adds that more research is needed into these treatments which could place major pressure on healthcare systems.

After decades of research, there's now a treatment that can be given to patients a single time.

James Paton, Healthcare journalist - Bloomberg

This one-shot therapy can potentially deliver a lifetime of benefits.

James Paton, Healthcare journalist - Bloomberg

Some of these treatments are getting approval from the Food and Drug Administration in the United States and the European Medicines Agency as well.

James Paton, Healthcare journalist - Bloomberg

There could be 10 to 20 of these cell and gene therapies getting approval every year.

James Paton, Healthcare journalist - Bloomberg

Listen to the discussion for more details:


This article first appeared on CapeTalk : New gene therapy fetches $1.8m for one shot, among costly 'miracle cures'


Recommended

by NEWSROOM AI
Read More
Former media exec molested 'hundreds' of boys and young men - Deon Wiggett

Former media exec molested 'hundreds' of boys and young men - Deon Wiggett

The final episode of Deon Wiggett's podcast series 'My Only Story' has been published in collaboration with News24.

District Six land claimants to discuss govt's proposed restitution plan

District Six land claimants to discuss govt's proposed restitution plan

The District Six Reference Group will hold a meeting on Saturday to outline the proposals that the government has put on the table.

Is southern Africa drought drying up Victoria Falls?

Is southern Africa drought drying up Victoria Falls?

Harare-based BBC journalist Shingai Nyoka gives a first-hand account of the devastating effect of the drought on Zimbabwe.

'We're ready and able to deal with increased online payments on Black Friday'

'We're ready and able to deal with increased online payments on Black Friday'

PayFast MD Jonathan Smit says the spread of technologies available should help mitigate risk of compromising payment systems.

Why life sentences aren't the solution to SA's rape crisis

Why life sentences aren't the solution to SA's rape crisis

The criminal justice system needs to take action against the scourge of rape in SA, but longer prison sentences aren't the answer.

Son of slain Cradock Four activist implicates FW de Klerk in father’s murder

Son of slain Cradock Four activist implicates FW de Klerk in father’s murder

To this day, no one has been prosecuted for the brutal murders of Fort Calata, Matthew Goniwe, Sparrow Mkhonto and Sicelo Mhlauli.

Popular articles
[VIDEO] Brawl allegedly in Kyalami Estate has social media in stitches

[VIDEO] Brawl allegedly in Kyalami Estate has social media in stitches

Khabazela shares some of the videos that went viral on Twitter and Facebook.